KONFIDENT Phase 3 Trial Global Expansion: Sebetralstat Pharmacokinetics and Pharmacodynamics in Japanese and Chinese Adults

Honda D, Iverson M, Hansen E, Hampton SL, Jhee S, Yoon E, Audhya PK, Smith MD, Yea CM, Hide M

APAAACI 2023

Investigating On-Demand Use of Oral Sebetralstat in Adults and Adolescents With Hereditary Angioedema: Multicenter, Double-Blind, Randomized, Placebo-Controlled, Phase 3 KONFIDENT Trial and Open-Label Extension Designs

Hide M, Audhya PK, Smith MD, Yea CM

JSA 2023

Evaluation of patient‐reported outcome measures for on‐demand treatment of hereditary angioedema attacks and design of KONFIDENT, a phase 3 trial of sebetralstat

Cohn DM, Aygören-Pürsün E, Bernstein JA, Farkas H, Lumry WR, Maurer M, Zanichelli A, Iverson M, Hao J, Smith MD, Yea CM, Audhya PK, Riedl MA

2023 Clinical and Translation Allergy

Sebetralstat, Investigational Oral On-Demand Treatment for HAE: KONFIDENT Trial Design

Aygören-Pürsün E, Zanichelli A, Cohn DM, Farkas H, Bernstein JA, Audhya PK, Smith MD, Yea CM, Lumry WR, Riedl MA, Maurer M

IWAA 2023

Short-Term Prophylaxis With Sebetralstat, an Investigational Oral On-Demand Treatment for Hereditary Angioedema, in KONFIDENT-S

Bernstein JA, Riedl MA, Lumry WR, Audhya PK, Smith MD, Yea CM

IWAA 2023

In Their Own Words – Patient Descriptions of the Earliest Recognition of HAE Attack Onset

Manning ME, Burnette AF, van Kooten S, Heckmann M, Danese S, Goga L, Guilarte M

HAEA National Summit 2023

Recognizing the Importance of Early On-Demand Treatment in the HAE Attack Journey

Jones DH, Ogbogu P, van Kooten S, Heckmann M, Danese S, Goga L, Magerl M

HAEA National Summit 2023

Preferences of People with Hereditary Angioedema for On-Demand Treatment: A US-Based Qualitative Study

Bukstein DA, Vibha Desai V, Goga L, Czado S, Brown M, Myers K, Audhya PK, Settipane RA, Busse PJ

HAEA National Summit 2023

PB0536: Oral Factor XIIa inhibitor KV998086 protects against FeCl3 induced thrombosis in mice.

Clermont A, Pinckney F, Hill M, Hampton SL, Feener EP

ISTH 2023

Understanding the complex decision-making associated with on-demand treatment of hereditary angioedema (HAE) attacks

Grumach A, van Kooten S, Heckmann M, Danese S, Goga L, Garcez T

EAACI 2023